Poster Presentation The 45th Lorne Conference on Protein Structure and Function 2020

Mechanisms of RNA-targeting by CRISPR-Cas13 (#412)

Gavin J Knott 1 , Akshay Tambe 1 , Dylan C Smock 2 , Brittney W Thornton 1 , Jennifer A Doudna 1 2 3
  1. Department of Molecular and Cell Biology, University of California, Berkeley, CA, USA
  2. Innovative Genomics Institute, University of California, Berkeley, CA, USA
  3. Howard Hughes Medical Institute, University of California, Berkeley, CA, USA

CRISPR-Cas (clustered regularly interspaced short palindromic repeats-CRISPR-associated) systems arose in bacteria and archaea as adaptive immune systems to combat foreign genetic elements. Cas13 (formerly C2c2) is an RNA-guided nuclease that base-pairs with complementary RNA to activate its higher eukaryotes and prokaryotes nucleotide-binding (HEPN) domains. Once activated, the HEPN domains will cleave bound target-RNA in cis and off-target single-stranded RNA in trans. Target-RNA dependent trans-cleavage by Cas13 has been harnessed to detect RNA in complex mixtures while cis-cleavage has been leveraged as a tool for specific RNA targeting in mammalian, plant, and yeast cells. Remarkably, the family of Cas13 enzymes are highly functionally and evolutionarily divergent; different orthologs target RNA with variable efficacy and diverged HEPN-nulceases show discrete RNA substrate preferences. Here, we describe our recent advances combining structural biology and high-throughput sequencing to better understand how divergent Cas13 enzymes negotiate complex RNA secondary structures, discriminate against mismatched target-RNA, and carry out catalysis.